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RARECast

En podcast av: RARECast

RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy

Our American listeners can also listen to RARECast at our American site

516 Avsnitt

A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Publicerades 2024-11-07

Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Publicerades 2024-10-31
Scaling N-of-1 Therapies to Viability
Publicerades 2024-10-24
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Publicerades 2024-10-17
How One Woman Climbed from Patient to Advocate
Publicerades 2024-10-10
Shortening the Diagnostic Odyssey
Publicerades 2024-10-03
Making Exomes More Revealing
Publicerades 2024-09-26
How One Patient Organization Catalyzed Drug Development
Publicerades 2024-09-19
Enabling On-Demand Therapies
Publicerades 2024-09-16
After Driving an N-of-1 Therapy for Her Son, an Advocate Turns to Helping Others
Publicerades 2024-09-05
Putting Rare Disease Organization in the Business of Drug Development
Publicerades 2024-08-29
Understanding the Many Questions Gene Therapies Raise
Publicerades 2024-08-22
A Test to Identify People Likely to Develop ALS
Publicerades 2024-08-15
How an Ultra-Rare Disease Patient Foundation Advanced a Gene Therapy
Publicerades 2024-08-08
Making the $10 Genome a Reality
Publicerades 2024-08-01
A No-Nonsense Effort to Develop a Therapy that Works Across Genetic Diseases
Publicerades 2024-07-25
Mapping a Perilous Journey with Humor
Publicerades 2024-07-18
Restoring Vision in Inherited Retinal Disease
Publicerades 2024-07-11
Bringing Genome Sequencing to Rural Populations
Publicerades 2024-07-04
Addressing a Blind Spot in Treatments for the Cornea
Publicerades 2024-06-27
Taking a Different Approach to Rare Epilepsies
Publicerades 2024-06-20
A Rare Disease Drug Developer Tries to Earn Its Stripes
Publicerades 2024-06-13
Using Plasma to Treat Rare Diseases
Publicerades 2024-06-06
Differentiating Gene Therapies through Regulatory Elements
Publicerades 2024-05-30
How One Patient Organization Leverages Research Investments
Publicerades 2024-05-23
Charging into the Storm
Publicerades 2024-05-16
A Gene Therapy Developer that Embraces Different Models for Reaching Patients
Publicerades 2024-05-09
Using Directed Evolution to Develop New Vectors for Genetic Medicines
Publicerades 2024-05-02
Addressing a Shortage of Genetic Counselors with AI
Publicerades 2024-04-25
A Small Molecule Therapy to Regenerate Muscle in People with DMD
Publicerades 2024-04-18
Forging a Faster Path for Gene Therapies
Publicerades 2024-04-11
Determining the Value of Rare Disease Therapies
Publicerades 2024-04-04
Buying and Building a Gene Therapy Presence
Publicerades 2024-03-28
A Clinical Trial Failure Derails a Promising Technology
Publicerades 2024-03-21
Helping People with Undiagnosed Rare Diseases Find Answers
Publicerades 2024-03-14
Speeding and Scaling the Development of Genome Editing Therapies
Publicerades 2024-03-07
Getting a Next-Generation Genome Editing Therapy for Sickle Cell Disease Back on Track
Publicerades 2024-02-29
Trying to Break a Leg in a Wheelchair
Publicerades 2024-02-22
A Drug Developer that Makes Pediatric Cancers a Priority
Publicerades 2024-02-15
Harnessing the Body’s Natural RNA Machinery to Treat Diseases
Publicerades 2024-02-08

RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

516 Avsnitt

A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter

Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection

Scaling N-of-1 Therapies to Viability

Building Gene Therapies that Address Gain and Loss of Function Simultaneously

How One Woman Climbed from Patient to Advocate

Shortening the Diagnostic Odyssey

Making Exomes More Revealing

How One Patient Organization Catalyzed Drug Development

Enabling On-Demand Therapies

After Driving an N-of-1 Therapy for Her Son, an Advocate Turns to Helping Others

Putting Rare Disease Organization in the Business of Drug Development

Understanding the Many Questions Gene Therapies Raise

A Test to Identify People Likely to Develop ALS

How an Ultra-Rare Disease Patient Foundation Advanced a Gene Therapy

Making the $10 Genome a Reality

A No-Nonsense Effort to Develop a Therapy that Works Across Genetic Diseases

Mapping a Perilous Journey with Humor

Restoring Vision in Inherited Retinal Disease

Bringing Genome Sequencing to Rural Populations

Addressing a Blind Spot in Treatments for the Cornea

Taking a Different Approach to Rare Epilepsies

A Rare Disease Drug Developer Tries to Earn Its Stripes

Using Plasma to Treat Rare Diseases

Differentiating Gene Therapies through Regulatory Elements

How One Patient Organization Leverages Research Investments

Charging into the Storm

A Gene Therapy Developer that Embraces Different Models for Reaching Patients

Using Directed Evolution to Develop New Vectors for Genetic Medicines

Addressing a Shortage of Genetic Counselors with AI

A Small Molecule Therapy to Regenerate Muscle in People with DMD

Forging a Faster Path for Gene Therapies

Determining the Value of Rare Disease Therapies

Buying and Building a Gene Therapy Presence

A Clinical Trial Failure Derails a Promising Technology

Helping People with Undiagnosed Rare Diseases Find Answers

Speeding and Scaling the Development of Genome Editing Therapies

Getting a Next-Generation Genome Editing Therapy for Sickle Cell Disease Back on Track

Trying to Break a Leg in a Wheelchair

A Drug Developer that Makes Pediatric Cancers a Priority

Harnessing the Body’s Natural RNA Machinery to Treat Diseases